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PPTA Responds to The Pharmaceutical Journal

In December 2017, The Pharmaceutical Journal published a correspondence piece that included a few misleading statements regarding the prospective use of gene therapy for treatment of common variable immune deficiency (CVID), when in reality, the treatment is only being discussed for a rare form of severe combined immunodeficiency caused by adenosine deaminase deficiency (SCID-ADA).

PPTA submitted a response to the original article with corrections to the original author's inaccuracies and misleading interpretations. The response article, "Keeping the record straight on the availability of gene therapy for common variable immunodeficiency," was published online last week.